A Phase 3, Randomized, Double-blind, Add-on Study Evaluating the Safety and Efficacy of Navtemadlin Plus Ruxolitinib vs Placebo Plus Ruxolitinib in Patients with Myelofibrosis Who Have a Suboptimal Response to Ruxolitinib

ID 2023-504724-25-00

Recrutement en cours

Date de révision : 27/04/2026

12 participants

Homme Femme

A partir de 18 ans

Date de début de recrutement : 09/04/2025

Critères :

Critères d'inclusion :

  • Ruxolitinib Run-In Period: 1. Adults ≥ 18 years of age able to provide informed consent.
  • Ruxolitinib Run-In Period: 2. Confirmed diagnosis of PMF, post-PV MF, or post-ET MF, as assessed by the treating physician according to the World Health Organization (WHO) criteria
  • Ruxolitinib Run-In Period: 3. High, Intermediate-1, Intermediate-2 risk category International Prognosis System Score (IPSS)
  • Ruxolitinib Run-In Period: 4. Eastern Cooperative Oncology Group (ECOG) performance status of 0 to 2.
  • Ruxolitinib Run-In Period: 5. JAK-inhibitor treatment naive
  • Randomized Add-on Period: 1. PMF, post-PV MF, or post-ET MF that is TP53WT as assessed by central testing.
  • Randomized Add-on Period: 2. ECOG performance status of 0 to 2.
  • Randomized Add-on Period: 3. Treatment with a stable dose of ruxolitinib
  • Randomized Add-on Period: 4. Suboptimal response to run-in ruxolitinib therapy

Critères d'exclusion :

  • Ruxolitinib Run-In Period: 1. Prior Splenectomy
  • Ruxolitinib Run-In Period: 2. Splenic irradiation within 3 months prior to the first dose
  • Ruxolitinib Run-In Period: 3. Prior BCL-XL, BET, MDM2, PI3K, PIM, or XPO1 inhibitors therapy or p53- directed therapy
  • Ruxolitinib Run-In Period: 4. Eligible for Bone Marrow Transplant
  • Ruxolitinib Run-In Period: 5. Peripheral blood or bone marrow blast count ≥ 10%
  • Randomized Period: 1. Peripheral blood or bone marrow blast count ≥ 10%

Lieux et contacts

Informations pratiques pour participer à cet essai.

Sites des essais

Adresse

Comment postuler ?

Pour participer à cet essai clinique, veuillez contacter la personne responsable de l'étude. Vous trouverez ses coordonnées dans la section "Lieux et contacts", puis "Contacts".

Avertissement

La sécurité et la validité scientifique de cette étude sont la responsabilité du sponsor de l'étude et des investigateurs.